UTROPHIN PROMOTER ACTIVITY UPREGULATION FOR THE T

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专利名称:UTROPHIN PROMOTER ACTIVITY
UPREGULATION FOR THE TREATMENT OF
MUSCULAR DYSTROPHY
发明人:KHURANA, Tejvir, S.,DIAMOND, Scott,
L.,MOORWOOD, Catherine,LOZYNSKA,
Olga,NAPPER, Andrew, D.,PISTILLI,
Emidio,SURI, Neha
申请号:US2009064230
申请日:20091112
公开号:WO10/056880P1
公开日:
20100520
专利内容由知识产权出版社提供
摘要:Methods are provided for increasing utrophin promoter activity, utrophin expression or utrophin activity, and treating or reducing the symptoms of muscular dystrophy by administering to a subject in need thereof an effective amount of a composition comprising a utrophin promoter or activity upregulator. Muscular dystrophy includes but is not limited to Duchenne muscular dystrophy, Becker's muscular dystrophy, limb girdle muscular dystrophy, or a disease characterized by mutation or dysregulation of the dystrophin gene or an aberrant or dysfunctional dystrophin.
申请人:KHURANA, Tejvir, S.,DIAMOND, Scott, L.,MOORWOOD, Catherine,LOZYNSKA, Olga,NAPPER, Andrew, D.,PISTILLI, Emidio,SURI, Neha
地址:3160 Chestnut Street-suite 200 Philadelphia, PA 19104-6283 US,1225 Greentree Lane Narnerth, PA 19072 US,610 Yale Road Bala Cynwyd, PA 19004 US,821 South St. Bernard Street Philadelphia, PA 19143 US,918 Pine Street #3m Philadelphia, PA 19107
US,910 Lamberhurst Close Chadds Ford, PA 19317 US,433 Carson Avenue Deptford, NJ 08096 US,4247 Locust Street, Apt. #102 Philadelphia, PA 19104 US
国籍:US,US,US,US,US,US,US,US
代理人:COHEN, Mark, S.
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